1. Duchenne muscular dystrophy and related dystrophinopathies: developing drugs for treatment Publication: Silver Spring, MD : Center for Drug Evaluation and Research, February 2018 Subject(s): Clinical Trials as Topic -- standardsDrug Evaluation -- standardsMuscular Dystrophies -- drug therapyMuscular Dystrophy, Duchenne -- drug therapyDrug Labeling -- standardsDrugs, InvestigationalResearch DesignHumansUnited StatesUnited States. Department of Health and Human Services.United States. Food and Drug Administration.
