Subjects: Clinical Trials as Topic and Genetic Therapy / Titles: Human gene therapy for rare diseases - Digital Collections - National Library of Medicine Search Results

Start Over Subjects Clinical Trials as Topic ✖ Subjects Genetic Therapy ✖ Titles Human gene therapy for rare diseases ✖

1. Human gene therapy for rare diseases

Publication:: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020
Subject(s):: Drug Development
Genetic Therapy
Rare Diseases -- therapy
Clinical Trials as Topic
Drug Evaluation, Preclinical
United States
United States. Department of Health and Human Services.
United States. Food and Drug Administration.