1. Human gene therapy for retinal disorders Publication: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020 Subject(s): Clinical Trials as TopicGenetic TherapyDrug Evaluation, PreclinicalRetinal Diseases -- therapyInvestigational New Drug ApplicationUnited StatesUnited States. Department of Health and Human Services.United States. Food and Drug Administration.
2. Human gene therapy for rare diseases Publication: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020 Subject(s): Drug DevelopmentGenetic TherapyRare Diseases -- therapyClinical Trials as TopicDrug Evaluation, PreclinicalUnited StatesUnited States. Department of Health and Human Services.United States. Food and Drug Administration.
3. Human gene therapy for hemophilia Publication: Silver Spring, MD : Center for Biologics Evaluation and Research, January 2020 Subject(s): Genetic TherapyHemophilia A -- drug therapyHemophilia B -- drug therapyClinical Trials as TopicDrug Evaluation, PreclinicalFactor VIII -- therapeutic useFactor IX -- therapeutic useUnited StatesUnited States. Department of Health and Human Services.United States. Food and Drug Administration.
