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- Publication:
- [Boston, Massachusetts] : Institute for Clinical and Economic Review, February 14, 2018
- Subject(s):
- Genetic Therapy
Leber Congenital Amaurosis -- genetics
Leber Congenital Amaurosis -- therapy
Retinal Diseases -- genetics
Retinal Diseases -- therapy
Retinal Pigment Epithelium -- abnormalities
Mutation
Randomized Controlled Trials as Topic
Treatment Outcome
Visual Acuity
Humans
United States
- Author(s):
- Beaudoin, Francesca L., author
Richardson, Marina, author
Synnott, Patricia G., author
Lancaster, Victoria, author
Fluetsch, Noemi, author
Herce-Hagiwara, Belén, author
Campbell, Jon D., author
Pearson, Steven D., author
Rind, David M., author
- Publication:
- [Boston, Massachusetts] : Institute for Clinical and Economic Review, July 19, 2022
- Subject(s):
- beta-Thalassemia -- therapy
Biological Products -- therapeutic use
Genetic Therapy
United States
- Author(s):
- Rind, David M., author
Walton, Surrey M., author
Agboola, Foluso, author
Herron-Smith, Serina, author
Quach, Danny, author
Chapman, Rick M., author
Pearson, Steven D., author
Bradt, Pamela, author
- Publication:
- [Boston, Massachusetts] : Institute for Clinical and Economic Review, November 20, 2020
- Subject(s):
- Antibodies, Monoclonal
Genetic Therapy
Hemophilia A -- drug therapy
United States
- Author(s):
- Ellis, Alexandra, author
Mickle, Kristin, author
Herron-Smith, Serina, author
Kumar, Varun M., author
Cianciolo, Laura, author
Seidner, Matt, author
Rind, David, author
Pearson, Steven, author
Thokala, P. (Praveen), author
Stevenson, M. (Matt), author
- Publication:
- [Boston, Massachusetts] : Institute for Clinical and Economic Review, May 24, 2019
- Subject(s):
- Genetic Therapy
Muscular Atrophy, Spinal -- drug therapy
United States
- Author(s):
- Beaudoin, Francesca, author
Nikitin, Dmitriy, author
Campbell, Jonathan D., author
McKenna, Avery, author
Pearson, Steven D., author
Rind, David M., author
Thokala, P. (Praveen), author
Spackman, David Eldon, author
- Publication:
- [Boston, Massachusetts] : Institute for Clinical and Economic Review, August 21, 2023
- Subject(s):
- Anemia, Sickle Cell -- therapy
Genetic Therapy
United States
- Author(s):
- Tice, Jeffrey A., author
Chu, Janet N., author
Moradi, Ashton, author
Herce-Hagiwara, Belen, author
Fahim, Shahariar Mohammed, author
Agboola, Foluso, author
Pearson, Steven D., author
Rind, David M., author
Walton, Surrey M., author
Sarker, Jyotirmoy, author
- Publication:
- [Boston, Massachusetts] : Institute for Clinical and Economic Review, December 22, 2022
- Subject(s):
- Antibodies, Bispecific
Antibodies, Monoclonal, Humanized
Cost-Effectiveness Analysis
Genetic Therapy
Hemophilia A -- therapy
Hemophilia B -- therapy
United States
