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Start Over Subjects Genetic Therapy ✖Remove constraint Subjects: Genetic Therapy Authors Thokala, P. (Praveen), author ✖Remove constraint Authors: Thokala, P. (Praveen), author

1. Spinraza and Zolgensma for spinal muscular atrophy: effectiveness and value : final evidence report

Author(s):
Ellis, Alexandra, author
Mickle, Kristin, author
Herron-Smith, Serina, author
Kumar, Varun M., author
Cianciolo, Laura, author
Seidner, Matt, author
Rind, David, author
Pearson, Steven, author
Thokala, P. (Praveen), author
Stevenson, M. (Matt), author
Publication:
[Boston, Massachusetts] : Institute for Clinical and Economic Review, May 24, 2019
Subject(s):
Genetic Therapy
Muscular Atrophy, Spinal -- drug therapy
United States

2. Gene therapies for sickle cell disease: final evidence report

Author(s):
Beaudoin, Francesca, author
Nikitin, Dmitriy, author
Campbell, Jonathan D., author
McKenna, Avery, author
Pearson, Steven D., author
Rind, David M., author
Thokala, P. (Praveen), author
Spackman, David Eldon, author
Publication:
[Boston, Massachusetts] : Institute for Clinical and Economic Review, August 21, 2023
Subject(s):
Anemia, Sickle Cell -- therapy
Genetic Therapy
United States