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Start Over You searched for: Subjects Genetic Therapy Remove constraint Subjects: Genetic Therapy Authors Herron-Smith, Serina, author Remove constraint Authors: Herron-Smith, Serina, author

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1. Valoctocogene roxaparvovec and emicizumab for hemophilia A without inhibitors: effectiveness and value : final report

2. Spinraza and Zolgensma for spinal muscular atrophy: effectiveness and value : final evidence report