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Start Over You searched for: Subjects Genetic Therapy Remove constraint Subjects: Genetic Therapy Authors Cianciolo, Laura, author Remove constraint Authors: Cianciolo, Laura, author Authors Thokala, P. (Praveen), author Remove constraint Authors: Thokala, P. (Praveen), author

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1. Spinraza and Zolgensma for spinal muscular atrophy: effectiveness and value : final evidence report