Subjects: Leber Congenital Amaurosis -- genetics and Retinal Diseases -- genetics / Languages: English - Digital Collections - National Library of Medicine Search Results

Start Over Subjects Leber Congenital Amaurosis -- genetics ✖ Subjects Retinal Diseases -- genetics ✖ Languages English ✖

1. Voretigene neparvovec for biallelic RPE65-mediated retinal disease: effectiveness and value : final evidence report

Publication:: [Boston, Massachusetts] : Institute for Clinical and Economic Review, February 14, 2018
Subject(s):: Genetic Therapy
Leber Congenital Amaurosis -- genetics
Leber Congenital Amaurosis -- therapy
Retinal Diseases -- genetics
Retinal Diseases -- therapy
Retinal Pigment Epithelium -- abnormalities
Mutation
Randomized Controlled Trials as Topic
Treatment Outcome
Visual Acuity
Humans
United States