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Start Over You searched for: Subjects Genetic Therapy Remove constraint Subjects: Genetic Therapy Authors Pearson, Steven D., author Remove constraint Authors: Pearson, Steven D., author Authors Rind, David M., author Remove constraint Authors: Rind, David M., author

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1. Betibeglogene autotemcel for beta thalassemia: effectiveness and value : final evidence report

2. Valoctocogene roxaparvovec and emicizumab for hemophilia A without inhibitors: effectiveness and value : final report

3. Gene therapies for sickle cell disease: final evidence report

4. Gene therapy for hemophilia B and an update on gene therapy for hemophilia A: effectiveness and value : final evidence report